Solid biosciences reports efficacy and safety data from the ongoing ignite dmd clinical trial and resumption of patient dosing in the 2e14 vg/kg cohort

- interim data from six patients provide evidence of a potential benefit of sgt-001 in functional endpoints of north star ambulatory assessments (nsaa), 6-minute walk test (6mwt), pulmonary function tests (pfts), and clinically validated patient reported outcome measures (proms) -
SLDB Ratings Summary
SLDB Quant Ranking