Generation bio presents data demonstrating first lipid nanoparticle to achieve uniform retinal transduction and tolerability via sub-retinal delivery of cedna and mrna at the european society of gene and cell therapy 2021 annual virtual congress

Sub-retinal delivery of closed-ended dna (cedna) using a retina-specific cell-targeted lnp (ctlnp) demonstrated broad photoreceptor distribution, durable expression and tolerability in rodents; potential to address inherited retinal diseases with full gene replacement
GBIO Ratings Summary
GBIO Quant Ranking